First Patients Treated in XLRP Gene Therapy Trial
Tuesday, September 17 2024 | 14 h 31 min | Vision Science
Beacon Therapeutics, has announced that they have treated the first patients in their Phase 2/3 VISTA trial for a gene therapy for X-linked retinitis pigmentosa (XLRP). The treatment, AGTC-501, is a gene replacement therapy and was originally developed by the company AGTC and then acquired by Beacon in 2023.
This trial is a global, randomized trial and will involve approximately 75 participants to test the efficacy and safety of the gene replacement therapy. Results from the trial will be shared in the coming years.
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